UK first to approve CRISPR treatment for diseases: what you need to know
Thank you for visiting nature.com. You are using a browser version with limited support for CSS. To obtain the best experience, we recommend you use a more up to date browser (or turn off compatibility mode in Internet Explorer). In the meantime, to ensure continued support, we are displaying the site without styles and JavaScript. Advertisement You can also search for this author in PubMed Google Scholar You have full access to this article via University of Michigan Library Sickle-cell anaemia is marked by red blood cells that are misshapen and sticky, affecting blood flow.Credit: Eye Of Science/SPL In a world first, the UK medicines regulator has approved a therapy that uses CRISPR gene editing as a treatment for diseases. The decision marks another high point for a biotechnology that has regularly been lauded as revolutionary in the decade since its discovery. The therapy, called Casgevy, will treat the the bl
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