Huntington's disease successfully treated for first time
One of the cruellest and most devastating diseases – Huntington's – has been successfully treated for the first time, say doctors. The disease runs through families, relentlessly kills brain cells and resembles a combination of dementia, Parkinson's and motor neurone disease. An emotional research team became tearful as they described how data shows the disease was slowed by 75% in patients. It means the decline you would normally expect in one year would take four years after treatment, giving patients decades of "good quality life", Prof Sarah Tabrizi told BBC News. The new treatment is a type of gene therapy given during 12 to 18 hours of delicate brain surgery. The first symptoms of Huntington's disease tend to appear in your 30s or 40s and is normally fatal within two decades – opening the possibility that earlier treatment could prevent symptoms from ever emerging. Prof Tabrizi, director of the University College London Huntington's Disease Centre, described the results as "spect
Huntington's disease successfully treated for first time 24 September 2025 Share Save Add as preferred on Google James Gallagher Health and science correspondent BBC/Fergus Walsh Professors Ed Wild and Sarah Tabrizi led the UK part of the trial One of the cruellest and most devastating diseases – Huntington's – has been successfully treated for the first time, say doctors. The disease runs through families, relentlessly kills brain cells and resembles a combination of dementia, Parkinson's and motor neurone disease. An emotional research team became tearful as they described how data shows the
Explore this link on the map →saved by
related reading
- Overview of Huntington’s Disease - Huntington's Disease Society of Americahdsa.org
- Medical breakthroughs in 2025 - by Saloni Dattaniscientificdiscovery.dev
- Understand - a novelette by Ted Chiangweb.archive.org
- Research Areas - Svendsen Lab | Cedars-Sinaicedars-sinai.edu
- Significantly Enhancing Adult Intelligence With Gene Editing May Be Possible — LessWronglesswrong.com
- Going Founder Mode On Cancer - by Elliot Hershbergcenturyofbio.com
- Neurosciences Seminar: X. William Yang, MD, PhD - Beyond the inherited CAG: Decoding a neuronal-selective pathogenic cascade in Huntington's disease | Wu Tsai Neurosciences Instituteneuroscience.stanford.edu
- FDA Approves First CRISPR Gene Editing Treatment for Sickle Cell Disease | Scientific Americanscientificamerican.com
- The Frontier in 2025renaissancephilanthropy.org
- ALS - Wikipediaen.wikipedia.org
- This baby boy was treated with the first personalized gene-editing drug | MIT Technology Reviewtechnologyreview.com
- It’s just a first step, but this new Alzheimer’s drug could be a huge breakthrough | Jonathan Schott | The Guardiantheguardian.com